Targeted lipid nanoparticles (LNPs) that can deliver mRNA-based gene editing therapeutics to hematopoietic stem cells (HSCs) in utero Problem: Monogenic blood diseases, including sickle cell disease and / thalassemia, are among the most prevalent genetic conditions worldwide, causing significant...
Tissue and Stem Cell Bank. FM Kirby Center for Molecular Ophthalmology. Stellar-Chance Labs 309 and 807. Philadelphia, PA 19104-6100. Vector Core Research Inquiries. IPSC Core Facility Research Inquiries. news.pennmedicine.org Inside Penn Medicine : Archives http://news.pennmedicine.org/inside...