In the current global pharmaceutical market, gene therapy drugs occupy a significant portion of the most expensive drug rankings, with five listed in the top ten. Pfizer's recently approved treatment for moderate to severe Hemophilia B, Beqvez, is priced at a staggering $3.5 million, making it...
该公司正在开发的基因疗法包括:1)AT132治疗X连锁肌小管性肌病,处于I/II期研究ASPIRO,去年10月公布的最新数据很有希望,该研究的下一次临床数据更新预计在今年5月;2)AT342治疗Crigler-Najjar综合征,处于I/II期研究VALENS,预计将于2019年第一季度对该项目进行更新;3)AT845治疗庞贝氏症(Pompe disease),处于IND启动阶...
细胞和基因疗法(Cell and Gene Therapy, CGT)是继小分子、大分子靶向疗法之后的新一代精准疗法。近年来,关于CGT领域的合作交易层出不穷,随着Big Pharma(国际性大药企)纷纷入场,推动着CGT行业快速发展。 据不完全统计,2024年1月,CGT重大合作交易就有10起,汇总如下: 1.诺华与Voyager 1月2日,Voyager Therapeutics发...
Top 10 Companies Leveraging Gene Editing in 2019 Bayer made much of its desire to establish a cell therapy pipeline on August 8, when it announced it would shell out up to $600 million to acquire full control of BlueRock Therapeutics. But the deal is just the latest example of growing .....
10. What is the future of gene therapy and how will it impact the pharmaceutical industry? The future of gene therapy is likely to be characterized by continued innovation, improved safety and efficacy, and increased commercialization efforts. This is expected to have a significant impact on the...
Gene delivery Cell therapy Influenza vaccine Biotechnology Plasmid Genomics Viral vector Expression vector Cancer vaccine ...[+17] Merck Patent GmbH 1668 | Germany | 10,000-50,000 | http://merckgroup.com | Merck (d.b.a. EMD Millipore in the U.S. and Canada) is a German chemical and...
314results aboutGenecompanies Sort by: Most relevant In biology, a gene is a sequence of nucleotides in DNA or RNA that encodes the synthesis of a gene product, either RNA or protein. During gene expression, the DNA is first copied into RNA. The RNA can be directly functional or be the...
Founded in 2000 in Shanghai, WuXi AppTec is the newest company in our top 10. It provides services across the entire development cycle including small molecule R&D and manufacturing, biologics R&D and manufacturing, cell and gene therapy. It currently operates in 18 locations across China, Icelan...
在快速发展的 生物医药 领域,细胞基因疗法(Cell & Gene Therapy,CGT)作为新兴的 精准医疗 手段,已经展现出巨大的潜力和市场前景。CGT概念提出至今已有半个多世纪,但相较于化学药物和生物靶向药,其发展仍处于相对早期阶段。然而,正是这一早期阶段,蕴含着无限的
Unlike other gene therapy companies, CRISPR doesn’t take an aggressive approach to differentiating itself from its competitors either. This company prioritizes valuable partnerships, actively seeking out and working with well-known organizations like Vertex and Bayer to achieve new things. ...