Unlike other gene therapy companies, CRISPR doesn’t take an aggressive approach to differentiating itself from its competitors either. This company prioritizes valuable partnerships, actively seeking out and working with well-known organizations like Vertex and Bayer to achieve new things. The company,...
In biology, a gene is a sequence of nucleotides in DNA or RNA that encodes the synthesis of a gene product, either RNA or protein. During gene expression, the DNA is first copied into RNA. The RNA can be directly functional or be the intermediate templat
Sangamo BioSciences is a clinical stage biopharmaceutical company involved in gene therapy that is researching ways of commercializing Zinc finger nucleases which modify a cell's DNA at an exact location thereby correcting or disrupting a specific gene. Sangamo BioSciences' lead therapy, SB-728, is ...
2023年6月22日,Sarepta的Elevidys获FDA批准,用于治疗4至5岁DMD儿童患者,成为全球首款获批上市的杜氏肌营养不良AAV基因疗法。此外,还有多款DMD靶点基因疗法临床进度较快,包括Genethon/Sarepta公司的GNT-0004,Pfizer的PF-06939926、BMB-001/BMB-D-001,Sarepta的Galgt2 genetherapy等。 DMD靶点基因疗法研发竞争格局 (2...
While biotech companies’ primary sphere of activity lies within the healthcare industry, by developing life-saving medicines and therapeutic solutions — including gene therapies and vaccines— the scope of their impact extends far beyond this. Biotech firms also venture into the realm of agriculture...
And gene therapy Zolgensma, launched to much attention last June for spinal muscular atrophy, has steadily gained market momentum, as payers haven’t shied away from backing the one-dose treatment despite its hefty price tag. Rounding out the top five Pharma 50 placeholders are Pfizer, Merck...
As we start 2022, we decided to take a look back at some of the largest mergers and acquisitions in 2021. The last 12 months were relatively quiet for M&As; however, there were some very interesting deals. Here are the top 10 M&As that made it through 20
The estimated global gene therapy market value is estimated to exceed $10 billion by 2025.. Analysts at Roots Analysis, a pharmaceutical research and consulting firm, predict the mRNA therapeutics and vaccine market will reach $10 billion in 2021. Researchers also found that 150 mRNA vaccines and...
Based on the Synthetic Biology Innovation Map, the Tree Map below illustrates the impact of the Top 10 Synthetic Biology Trends in 2025. Gene and cell therapy are at the forefront of synthetic biology, with techniques like CAR-T cell therapy creating better cancer treatments, among others. CRISP...
In the end, if you’re looking for biotech stocks to buy that are looking at gene therapy, CRISPR Therapeutics could be a major star. uniQure NV (QURE) Source: Shutterstock When it comes to biotech stocks,uniQure(NASDAQ:QURE) is gene therapy royalty. That’s because the firm actually cr...