美国当地时间2024年9月17日,美国食品药品监督管理局(FDA)正式批准了瑞风生物针对Usher综合征的创新药物RM-101的IND申请。这一批准标志着Usher综合征全球首个基于AAV的基因编辑药物研发取得了里程碑式的突破与进展。视网膜色素变性是一组遗传性眼科疾病,主要特征为视网膜光感受器细胞的进行性退化,导致视力逐渐丧失。Usher...
Alice is a 1982 musical-fantasy film co-produced by Belgian and Polish film companies. The film is a modern telling of Lewis Carroll's Alice's Adventures in Wonderland story and stars French actress Sophie Barjac in the title role. Jean-Pierre Cassel plays the jogger named Rabbit with whom...
The Complete List of Global Health Tech Unicorns Global Health Tech Unicorns A unicorn startup or unicorn company is a private company with a valuation over $1 billion USD. Unicorns are ‘startups’, i.e they do not include post-exit, acquired or listed companies, nor do they include ‘...
ADAGE – Analysis using Denoising Autoencoders of Gene Expression[github] This is a Theano implementation of stacked denoising autoencoders for extracting relevant patterns from large sets of gene expression data, a kind of feature construction approach if you will. I have played around with this...
Bayesian analysis of gene knockout screens using pooled library CRISPR or RNAi. CaRpools - [R] - A pipeline for end-to-end analysis of pooled CRISPR/Cas9 screening data. Including in-depth analysis of screening quality and sgRNA phenotypes. casTLE - [Python] - Based on the empirical ...
uniquely positioned in a dense urban environment in the heart of University City. Anticipated to be complete in 2026, the 500,000 square foot six-story facility will also serve as a center of excellence for Roche gene therapy manufacturing globally, with the ability to flex and adapt t...
Actagene Oncology Acquired by Ignyta May 2013 Actavalon Shut down Dec 2020 Actavis Acquired Allergan, $70B, Took Allergan name Actelion Clinical Research Was part of Actelion Pharmaceuticals Actelion Pharmaceuticals Acquired by J&J, Jun 2017, $30B Actera Pharmaceuticals Closed Actient Pharmaceuticals Acq...
James Watson, Francis Crick, and Rosalind Franklin on the structure of DNA, which in turn made it possible for geneticists to crack the DNA code of all organisms.In his later years he promoted nuclear disarmament, as well as orthomolecular medicine, megavitamin therapy...
Wed, 30 Oct - Fri, 01 Nov 2024 Gene Therapy Analytical Development Boston Join the 5th Annual Gene Therapy Analytical Development Summit to discuss the latest analytical tools ensuring safety, efficacy, quality, and consistency of gene therapy products ...
Hangzhou Future Sci-Tech City has long since become a well-deserved "source of global innovation". In recent years, the world's leading high-tech companies have settled here, gathering young scientific and technological talents from all over the world. The following is the list of 2021 MIT ...