Paroxysmal nocturnal hemoglobinuria (PNH) is a very rare disease. It’s also very complex. If you or a loved one has recently been diagnosed with PNH, you may wonder what sort of challenges you will face. It’s hard to know right away. Sometimes, people with PNH have few, if any, ...
Based on an improved overall survival of PNH patients with a sufficient complement inhibition, it could be speculated that in context with the natural history of the disease, the number of combined PNH-bone marrow failure cases will increase in the coming years. Thus, the optimizing of ...