[0057]AAV9‑01Mut‑GFP是指基于修饰腺相关病毒血清型9(rAAV9)的载体,其包含具有突 变F422W的修饰AAV9衣壳蛋白VP1。 [0058]AAV9‑02Mut‑GFP是指基于修饰腺相关病毒血清型9(rAAV9)的载体,其包含具有突 变I601M的修饰AAV9衣壳蛋白VP1。 [0059]AAV9‑03Mut‑GFP是指基于修饰腺相关病毒血清型9(...
There were no antibodies against GFP in ewes or lambs. Analysis of fetal gonads demonstrated GFP expression in female (but not male) germ cells, with low levels of integration-specific reads, without integration in select proto-oncogenes. These results suggest potential therapeutic benefit of AAV9...
常见的广谱型启动子CMV、CAG 可在心脏中高效表达,如果特异性要求不高,可以选择CMV 启动子,其对心脏的转导效率很高。 AAV9-CMV与AAV9-CBA 介导心肌中GFP 表达结果(Chen et al., Clin Exp Pharmacol Physiol, 2015) 若要实现目的基因在心脏中特异性表达,推荐选择心脏特异性的启动子,如cTNT、αMHC、Des、MLC2v...
42 Titers were calculated by qPCR with GFP primers (F5′-AGAACGGCATCAAGGTGAAC-3′, R 5′-GAACTCCAGCAGGACCATGT-3′), ITR primers (F 5′-GACCTTTGGTCGCCCGGCCT-3′, R 5′-GAGTTGGCCACTCCCTCTCTGC-3′), human growth hormone (hGH) primers (F 5′-TGGGAAGACAACCTGTAGGG-3′, R 5′...