Gene therapy is designed to treat diseases by introducing exogenous DNA or RNA into human target cells, which may be achieved by a few different methods. It is used to treat inherited genetic disorders: to correct or compensate for the patient’s abnormal gene, or to silence or inhibit the ...
Allogeneic bone marrow transplantation, immunoglobulin and enzyme replacement treatments and more recently gene therapy have all been introduced into clinical medicine as treatments for one or more of the primary immunodeficiency diseases. Beginning in 1990, gene-corrected T cells were first used to ...
It used to be that Inherited Retinal Diseases were a type of diagnosis one was given, and there was not much hope in terms of treatment. A lot of patients would progressively lose vision and had to rely on low vision devices. But these days, we do have an approved gene the...
Genetic testing: This test looks for disease-causing mutations in the GLA gene, and is the most reliable way to diagnose Fabry in all patients. Fabry disease genetic testing can also be used to identify the disease in other family members once a person is diagnosed....
A change in the therapeutic landscape has been achieved for many chronic or previously incurable diseases over the last decade. Antisense oligonucleotide or gene replacement therapy for patients with spinal muscular atrophy (Weiß et al. 2022) and the recent approval of aducanumab and lecanemab fo...
The Unites States Navy also heavily used asbestos in the construction of ships and vessels. As a result, thousands of shipyard workers and Navy veterans have been diagnosed with asbestos-related diseases. What cancers are caused by asbestos exposure?
Whole genome sequencing is a laboratory process that examines a person's DNA makeup in order to provide information about the risk for developing diseases in the future, as well as to diagnose active symptoms or diseases. Currently, the technology is most commonly used to find a medical cause...
Medical professionals are using gene therapy to treat various cancers, hereditary diseases caused by a genetic defect, human immunodeficiency virus (HIV) and other diseases. The technique works best with diseases that are caused by single defective genes. Many chronic diseases are caused by multiple ...
Coats’ eye disease is considered an idiopathic condition. Researchers don’t know exactly what causes it. This condition is one of a number of rare eye diseases that result from blood vessel problems in your eye. Similar conditions include Norrie disease and persistent fetal vasculature (PFV). ...
Myostatin gene mutation with follistatin vaccine = 4 times the muscle If follistatin works in humans, not only will muscular degenerative diseases have a cure, but sports and bodybuilding would have a new “natural” steroid. If you think Barry Bonds’ head is big, just wait until Ronnie Colem...