获得PRIME资格的药物,必须有初步临床证据和非临床证据表明该药与现有治疗药物相比能够实质性改善病情。 SCD(图片来源:nursingcrib.com) CTX001是一种在研的、自体、体外CRISPR/Cas9基因编辑疗法,目前正在评估用于治疗输血依赖性β地中海贫血(...
Mary Etta C. Mills, RN, ScD, CNAA, Baltimore, MD and Diane S. Pravikoff, RN, PhD, Glendale, CA, were inducted as Fellows in the American Academy of Nursing October 27, 2001 in Washington, DC
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