Global reach and impact: IQVIA's rare disease solutions span thousands of clinical sites worldwide, ensuring broad access and efficient trials. Your work brings hope to over 350 million people affected by more than 7,000 rare diseases. Clinical delivery expertise: Our team includes highly experie...
The Rare Diseases Clinical Research Network: a model for clinical trial readinessdoi:10.1177/26330040231219272Lumsden, Joanne M.Urv, Tiina K.Therapeutic Advances in Rare Disease
The TANGO study aims to create a large international network of centers to study glomerular disease (GN) recurrence after renal transplantation. Currently Enrolling Interventional EPPIK (FSGS & MCD) The EPPIK study will evaluate the investigational drug, sparsentan, for the treatment of selected rare...
Worldwide clinical trial support with precise expertise for specific regulatory and clinical needs Commitment to innovation A relentless pursuit of diagnostic advancements to overcome rare disease challenges Regulatory Our experienced regulatory team supports a broad range of submissions, including 510(k) and...
The figure also outlines the contributions of different entities including connect 4 children (C4C), European Federation of Pharmaceutical Industries and Associations (EFPIA), European Clinical Research Infrastructure Network (ECRIN), European Organisation for RD (EURORDIS), and European Rare Disease ...
INTRODUCTION TO THE RARE DISEASE CONSORTIUM NETWORK AND THE UCDC: INDUSTRY RELATIONSHIPS In response to the Rare Diseases Act of 2002, the National Institutes of Health (NIH) established the Rare Diseases Clinical Research Network (RDCRN) to address the unique challenges of performing research on ra...
Rare disease researchis difficult due to the scarcity of patient information on the conditions. Because there are so few people affected, patient recruitment for clinical studies might be very difficult. To address these difficulties, a number of charities, patient advocacy organizations, and government...
In-Network Services We are an in-network provider with most commercial health insurance plans. Interested In Partnering? Contact Us Specialties Rare Disease Cardiology Pediatrics Oncology Services Genetic Counseling Genetic Test Ordering Clinical Trial Matching & Recruitment ...
84 To achieve this goal, NORD and the Rare Disease Clinical Research Network (RDCRN)85 at the National Center for Advancing Translational Sciences (NCATS) have curated RD registries that are available for patients, researchers, and clinicians.86 Such registries not only facilitate communication ...
and articles on public health issues in the field of rare diseases and orphan drugs. The journal does not accept case reports which do not present clinical or pathological findings that can provide information about the mechanisms of a disease. Case reports which just present phenotype information,...