Stevens, Toward PKU enzyme replacement therapy: PEGylation with activity retention for three forms of recombinant phenylalanine hydroxylase, Mol. Ther. 9 (2004) 124-129.Gamez, A, Wang, L, Straub, M, Patch, MG, Stevens, RC (2004) Toward PKU enzyme replacement therapy: PEGylation with ...
Results on data on patients affected by Lysosomal disorders (LSD) were collected from March to June 2020 in UK where patients experienced the interruption of the home enzyme replacement treatment (ERT) infusions for a duration of 12 weeks during the first phase of COVID-19 pandemic. By means ...
This role will have a high degree of visibility across commercial leadership, local and regional partners, and functional leadership outside of commercial; and will play a key role in implementing a new commercial operating model and elevating the role of Commercial and our Brands within th...
Phenylketonuria (PKU) is an inherited deficiency in the enzyme phenylalanine hydroxylase (PAH), which, when poorly-managed, is associated with clinical features including deficient growth, microcephaly, seizures, and intellectual impairment. The manageme