New gene drug therapy found to help prostate cancerThe latest research into prostate cancer is producing several promising new treatments, including...Beavers, NormaDrug Topics
A new gene therapy for sickle cell disease has been deemed safe by a U.S. Food and Drug Administration advisory panel, paving the way for full approval by early December 2023. Ad The FDA had already decided that the therapy, known as exagamglogene autotemcel (exa-cel), was effective. ...
A team of Chinese scientists have developed a gene therapy that they say reverses some aspects of aging — and extend lifespans — in mice, Reuters reports. While plenty more research still needs to be done, the research sheds light on the underlying processes involved in aging, and reveals ...
The Food and Drug Administration said the one-time treatments can be used for patients 12 and older with severe forms of the disease. One, made by Vertex Pharmaceuticals and CRISPR Therapeutics, is the first approved therapy based onCRISPR,the gene editing toolthatwon its inventors the Nobel ...
Highlighting the benefits of this innovative approach, senior investigator of the Center for Genetic Medicine Research at Children’s National Hospital, Jyoti K Jaiswal, MSc PhD, commented, “Currently, patients with LGMD2B have no gene or drug-based therapies available to them, and we are ...
20 issue of Science Translational Medicine, researchers at NewYork-Presbyterian Hospital/Weill Cornell Medical Center say animal and human data suggest gene therapy to the brain may be able to treat patients with major depression who do not respond to traditional drug treatment.mnthealthnews...
A novel gene modulation system was identified within mammalian introns, regulating intracellular gene transcripts homologous to certain 5'-proximal non-snRNP-binding regions of spliced introns. This gene modulation system can be manipulated for the analysis of gene function and development of gene-specifi...
WASHINGTON, May 10 (Xinhua) -- A team of cancer researchers managed to exploit a vulnerability in melanoma that has developed resistance to a targeted therapy, providing a potential new therapeutic strategy to selectively kill the drug-resistant cancer cells. ...
By nine weeks old, mice that carry the mutant SOD1 gene are already showing molecular signs of deteriorating neuromuscular function. To find out whether the drug could reverse this decline, researchers treated 9-week-old mice with an anti-SOD1 oligo or a placebo. Muscle function steadily improv...
With 54 new drugs and seven cellular and gene therapy products, the approvals by the US Food and Drug Administration (FDA) recovered 2023 from the 2022 den