It has taken the lead in conducting research in fields such as medical aesthetics, specialty food, cell and gene therapy drugs, filling multiple gaps at home and abroad. Relying on the Leadingpharm CXO service system, Deep Blue Ocean has created an "interactive" clinical service model, fully ...
First Clinical Trial Of Gene Therapy For Muscular Dystrophy Lends Insight Into The DiseaseTom Hughes
The first clinical trial to test a revolutionary treatment for blindness in children has been announced by researchers at UCL (University College London). The trial, funded by the Department of Health, is the first of its kind and could have a significant impact on future treatments for eye di...
Purpose of reviewConsistently measurable and persistent expression of circulating clotting factor activity, associated with decreased clinical bleeding, has been achieved for the first time in a hemophilia gene therapy trial. This review examines the successes and limitations of this clinical trial for hem...
[2] Results from GALILEO-1, a first-in-human clinical trial of FLT201 gene therapy in patients with Gaucher disease Type 1. Retrieved May 9, 2024 from https://freeline.life/wp-content/uploads/Freeline-GALILEO-1-Results-ASGCT2024-Final-Presentation.pdf...
First Analysis exits portfolio company 4G Clinical as part of $230 million transaction First Analysis, a leading venture capital investor, recently successfully exited its investment in portfolio company 4G Clinical, a leader in randomization and clinical trial supply management (RTSM) technology, as ...
In the U.S., Vertex has not released a potential price for the therapy, but a report by the nonprofit Institute for Clinical and Economic Review said prices up to around $2 million would be cost-effective. By comparison, research earlier this year showed medical expenses for current sickle ...
Metastatic or non-resectable (stage IV) pancreatic cancer has a rapidly fatal outcome (median survival: 3-6 months), thus making gene therapy a viable therapeutic option. The objectives of the clinical studies are to evaluate the safety/toxicity and potential anti-tumor response/efficacy of intrav...
[2] Results from GALILEO-1, a first-in-human clinical trial of FLT201 gene therapy in patients with Gaucher disease Type 1. Retrieved May 9, 2024 from https://freeline.life/wp-content/uploads/Freeline-GALILEO-1-Results-ASGCT2024-Final-Presentation.pdf...
WASHINGTON, Nov. 6 (Xinhua) -- The first clinical trial in the United States showed that it appeared safe to genetically edit a cancer patient's immune cells using CRISPR-Cas9 technology before infusing those cells back into the patient, said a news release on Wednesday. ...