Quek DQ1, Nguyen LN2, Fan H3, Silver DL4. Author information Major Facilitator Superfamily Domain containing 2A (Mfsd2a) was recently characterized as a sodium-dependent lysophosphatidylcholine (LPC) transporter expressed at the blood-brain barrier endothelium. It is the primary route for importation...
He feels that can scale up to using organoids to develop more cure based models FDA Christine Nguyen MD regulatory perspective of framework of drug approval for rare diseases 1 in 10 Amercians have rare diseases; 70% genetic and half are children Due to Orphan Drug Act in 2023 half of no...
The author wishes to acknowledge the assistance of Jacqueline M. Kraft, PharmD, Ngoc Diem Nguyen, PharmD, and Phillipa Scheele, PharmD, PGY1 Residents, and Michael P. Conley, PharmD, and Nga T. Pham, PharmD, CDE, AE-C, Assistant Clinical Professors at Northeastern University — School ...
L. Chui, J. Gordon, J. L. Guthrie, F. B. Jamieson, D. Langlois-Klassen, R. Long, D. Nguyen, W. Wobeser, and M. W. Feldman. 2011.Dispersal ofMycobacterium tuberculosisvia the Canadian fur trade.Proc. Natl. Acad. Sci. USA108: 6526–6531. ...
“Herman’s lifelong pursuit of science, even to the very last day of his life, has been an inspiration to many of us,” says Chen, the Ivan R. Cottrell Professor of Immunology. “He was a great human being with a great attitude and a clear mind. He will be missed greatly.” ...
Christine Nguyen, FDA 10:00-10:20 FDA’s Regulatory Flexibility Beyond One Positive Adequate & Well-Controlled Trial (CME Eligible) Frank Sasinowski, Hyman, Phelps & McNamara 10:20 – 10:50 Networking, Exhibits and Product Presentations 10...
FDA Christine Nguyen MD regulatory perspective of framework of drug approval for rare diseases 1 in 10 Amercians have rare diseases; 70% genetic and half are children Due to Orphan Drug Act in 2023 half of novel drugs approved for rare diseases CDER and FDA 550 unique drugs for over 1000 ...
Ross Professor of Medicine, Professor of Gene & Cell Medicine, Director of the Cardiology Fellowship Program, and Co-Director of the Transatlantic Cardiovascular Research Center, which combines Mount Sinai Cardiology Laboratories with those of the Universite de Paris – Madame Curie. He earned a ...
Kraft, PharmD, Ngoc Diem Nguyen, PharmD, and Phillipa Scheele, PharmD, PGY1 Residents, and Michael P. Conley, PharmD, and Nga T. Pham, PharmD, CDE, AE-C, Assistant Clinical Professors at Northeastern University — School of Pharmacy and Harbor Health Services, Inc., Boston, ...