Gene therapy is a potentially potent new method of treating a number of neurologic disorders previously considered refractory to current conventional therapeutic treatments. Numerous advances have been made in the construction of expression vectors, cellular and viral transgene carriers, and the characterizat...
Scientist says gene therapy wastes time and money.(Brief Article)O'Leary, Cathy
This book addresses the important issue of gene therapy in human disease states. Gene therapy, which implies introduction of novel genes and inhibition of
Gene therapy + editing AAV Metagenomics Sequencing methods RNA sequencing Whole genome sequencing Targeted sequencing Epigenetics Public health + surveillance Liquid biopsy HiFi difference Bioinformatics Computational tools Haplotype Genomic sequencing Repeat expansions Agrigenomics Corporate...
laboratory through a LOEWE Cell and Gene Therapy (CGT) grant, SFB834 funding, LOEWE OSF and Frankfurt Autophagy Network (FAN) funding. S.S. is the recipient of a fellowship from the Faculty of Medicine of the Goethe University, Frankfurt am Main. Author information Authors and Affiliations ...
Adoptive immunotherapy using TCR gene modified T cells may allow separation of beneficial Graft versus tumour responses from harmful GvHD. Improvements to this include methods to generate high avidity or high affinity TCR, improvements in vector design and reduction in mispairing. Following adoptive ...
Tight control of gene expression in mammalian cells by tetracycline-responsive promoters. Proc. Natl Acad. Sci. USA 89, 5547–5551 (1992). Article CAS PubMed PubMed Central Google Scholar Guy, C. T., Cardiff, R. D. & Muller, W. J. Induction of mammary tumors by expression of ...
This chapter discusses several core problems of risk communication for the purpose of developing information strategies with regard to gene therapy, an emerging technology characterized by uncertainty in scientific knowledge with regard to benefits and risks. A major precondition for making responsible and...
基因治疗(gene therapy)是指将外源正常基因导入靶细胞,以纠正或补偿因基因缺陷和异常引起的疾病,以达到治疗目的。也包括转基因等方面的技术应用。也就是将外源基因通过基因转移技术将其插入病人的适当的受体细胞中,使外源基因制造的产物能治疗某种疾病。目前,基因治疗已经被用于治疗许多疾病。 2015年9月《Nature Genetics...
RNA therapy refers to the treatment or prevention of diseases using RNA-based molecules. The recent advent of a series of effective messenger RNA-based vaccines in response to the COVID-19 pandemic has reignited research interest in RNA therapy. Based on