Therapeutic protein and molecule delivery to target sites by transplanted human stem cells holds great promise for ex vivo gene therapy. Our group has demonstrated the therapeutic benefits of ex vivo gene therapy targeting the skeletal muscles in a trans
The ALS Association advocates for people living with ALS, funds ALS research, and offers a variety of resources to people with ALS and their families and caregivers. The association has chapters in several U.S. states. Search online for yourlocal state chapter. ALS Therapy Development Institute ...
Jason Chua, MD, PhD, is an assistant professor in the Department of Neurology and Division of Movement Disorders atJohns Hopkins School of Medicine. He received his training at the University of Michigan, where he obtained medical and graduate degrees, then completed a residency in neurology and...