[0051]EGFP是编码修饰绿色荧光蛋白的序列, 多聚A是多聚腺苷酸化信号, ITR是腺相关病毒的反向末端重复, HBG内含子是人β‑珠蛋白内含子, CMV启动子是人巨细胞病毒启动子, AmpR是β‑内酰胺酶基因的序列,其提供大肠杆菌对氨苄青霉素的抗性, pUC起点是高拷贝细菌复制起点。 [0052]图3是旨在用于从随机变体文库...
To first test the efficacy of dual vector delivery with AAV9-PHP.B, we generated AAV2/9-PHP.B-CMV-turbo red fluorescent protein (RFP)-WPRE (PHP.B-RFP) and coinjected this vector with AAV2/9-PHP.B-CMV-EGFP-WPRE at a 1:1 gc ratio in a total volume of 1 μL into the utricle...